Muscular Dystrophy Association Marks Rare Disease Day by Spotlighting Community Stories Driving Progress in Research, Care, and Advocacy

Muscular Dystrophy Association Marks Rare Disease Day by Spotlighting Community Stories Driving Progress in Research, Care, ...
Medical Xpress

Musculoskeletal Diseases: News and Research on Muscular Dystrophies

If cancer is a disease of overabundance, where cells divide without restraint and tumors grow despite the body's best interests, then degenerative diseases are disorders of deprivation. When ...
Business Insider

Muscular Dystrophy Association Announces nearly $2 Million in Collaborative Research Grants Advancing Treatments Across Multiple Neuromuscular Diseases

New York, Dec. 03, 2025 (GLOBE NEWSWIRE) -- The Muscular Dystrophy Association (MDA) today announced the awarding of seven new collaborative research grants totaling nearly $2 million to advance ...
Medical Xpress

Nervous System Diseases: News and Research on Muscular Diseases

A systematic review of research spanning 34 years has found a biological link between two common neurological conditions that can potentially save the NHS millions by streamlining treatments that ...
Nasdaq

Capricor Therapeutics Receives Orphan Drug Designation for Deramiocel in Becker Muscular Dystrophy, Expanding Focus in Neuromuscular Diseases

Capricor Therapeutics announced that the U.S. FDA has granted Orphan Drug Designation to its lead cell therapy candidate, Deramiocel, for the treatment of Becker Muscular Dystrophy (BMD). This ...
EurekAlert!

Genethon signs licensing agreement with AskBio for the development of an investigational gene therapy for Pompe disease

Genethon, a leading laboratory in gene therapy for rare diseases, today announced that it has entered into an exclusive, worldwide licensing agreement with AskBio, a gene therapy company wholly owned ...